Duchenne Muscular Dystrophy Therapies: The Path Forward Beyond Exon-Skipping Duchenne muscular dystrophy is a rare, progressive neuromuscular disorder caused by mutations in the dystrophin gene. While exon-skipping therapies have significantly shaped the Duchenne muscular dystrophy market, researchers are now actively exploring alternative approaches to enhance treatment outcomes.
Current Treatment Options for Duchenne Muscular Dystrophy (DMD) Patients...
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